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Looking for a way to send some holiday cheer? Try dropping a line to Lucas Hoelscher, a 14-year-old Springfield resident with spinal muscular atrophy type I. Lucas, who is unable to talk or move, enjoys receiving letters and cards in the mail because his life completely revolves around his visual skills. He can only communicate by making sounds or moving his eyes. Lucas, part of triplet sons ...
CARLSBAD, Calif., Nov. 22, 2013 /PRNewswire/ -- Isis Pharmaceuticals, Inc. (ISIS) announced today that it plans to add a 12 mg cohort to the ongoing Phase 1b/2a study evaluating ISIS-SMNRx in children with spinal muscular atrophy (SMA). In addition, a 12 mg dose will be included in an open-label extension study for those children who have completed dosing in previous studies. The addition of ...
Attendees of the 16th Annual Spinal Muscular Atrophy Angels Charity Ball enjoyed dinner, dancing and a live and silent auction at the Savannah Marriot Riverfront on Saturday evening.
Carlsbad-based Isis rose 8% Friday on news about its drug for spinal muscular atrophy.
Trophos SA, a clinical stage pharmaceutical company developing innovative therapeutics from discovery to clinical validation for indications with under-served needs in neurology and cardiology, has completed its efficacy study of olesoxime in the rare neurodegenerative condition Spinal Muscular Atrophy.
CARLSBAD, Calif., Nov. 12, 2013 /PRNewswire/ -- Isis Pharmaceuticals, Inc. (ISIS) announced today that it has earned a $1.5 million milestone payment from Biogen Idec related to the advancement of the ongoing Phase 2 study of ISIS-SMNRx in infants with spinal muscular atrophy (SMA). The Phase 2 study of ISIS-SMNRx is an open-label, multiple-dose, dose-escalation pilot study in infants who have ...
Bill authorizes the National Institutes of Health (NIH) to support the creation of up to 20 pediatric research consortia focused on diseases such as Spinal Muscular Atrophy. (PRWeb November 13, 2013) Read the full story at http://www.prweb.com/releases/nprna/spinalmuscularatrophy/prweb11332948.htm
It didn't take long for Erika Dmeza and her husband, William Trespo, to realize that their oldest son, Eryk Dmeza, was special.
FUN OF THE FAIR: Families were invited to help decorate a charity's Christmas tree as part of its festive fair at the weekend. The Donna Louise Children's Hospice staged the event on Saturday to help raise vital funds for the service. Hospice counsellor and artist, Kevin Benson, was encouraging guests to paint their very own Christmas bauble on a large canvas to help prepare the Trentham Lakes ...
JOHOR BAHARU, 14 Nov (Bernama) -- Biarpun menderita penyakit ketidakupayaanotot sejak dilahirkan, namun itu tidak menghalang Mohammad Harith Zakry dariSekolah Kebangsaan Datuk Usman Awang, Kota Tinggi untuk mencapai keputusancemerlang peperiksaan Ujian Penilaian Sekolah Rendah (UPSR).Beliau yang menderita penyakit spinal muscular atrophy (SMA) sehinggaterpaksa berkerusi roda berjaya mendapat ...
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